• Eteplirsen은 근육 단백질 디스트로핀 유전자의 특정 돌연변이 (결함)가 사람을 치료하는 개발 실험 약물이다.
• Sarepta 현재 등록 오픈 여러 사이트를 가지고 있으며, 38 사이트 (PROMOVI 연구라고도 함) 재판에 참여하도록 노력하고 있습니다.
eteplirsen 임상 3차에 참여독려 기사가 올라왔습니다. 엑손스킵 51번입니다.
임상 사이트는 아래와같습니다. 전부 미국지역입니다.
United States, Arizona | |
Neuromuscular Research Center | Recruiting |
Phoenix, Arizona, United States, 85028 | |
Contact: Beth Lasala 480-314-1007 Beth@nrcaz.com | |
Principal Investigator: Kumaraswamy Sivakumar, MD | |
United States, California | |
Not yet recruiting | |
Los Angeles, California, United States | |
Not yet recruiting | |
Sacremento, California, United States | |
Not yet recruiting | |
San Diego, California, United States | |
Not yet recruiting | |
Stanford, California, United States | |
United States, Colorado | |
Not yet recruiting | |
Aurora, Colorado, United States | |
United States, Connecticut | |
Not yet recruiting | |
Hartford, Connecticut, United States | |
United States, District of Columbia | |
Not yet recruiting | |
Washington, District of Columbia, United States | |
United States, Florida | |
Not yet recruiting | |
Gainesville, Florida, United States | |
Not yet recruiting | |
Gulf Breeze, Florida, United States | |
Not yet recruiting | |
Miami, Florida, United States | |
Not yet recruiting | |
Orlando, Florida, United States | |
United States, Georgia | |
Not yet recruiting | |
Atlanta, Georgia, United States | |
United States, Illinois | |
Not yet recruiting | |
Chicago, Illinois, United States | |
United States, Iowa | |
University of Iowa Children's Hospital | Recruiting |
Iowa City, Iowa, United States, 52242 | |
Contact: Carrie Stephan 319-356-2673 carrie-stephan@uiowa.edu | |
Principal Investigator: Katherine Mathews, MD | |
United States, Kansas | |
Not yet recruiting | |
Kansas City, Kansas, United States | |
United States, Maryland | |
Not yet recruiting | |
Baltimore, Maryland, United States | |
United States, Massachusetts | |
Not yet recruiting | |
Boston, Massachusetts, United States | |
United States, Michigan | |
Not yet recruiting | |
Detroit, Michigan, United States | |
United States, Minnesota | |
Not yet recruiting | |
Minneapolis, Minnesota, United States | |
United States, Missouri | |
Not yet recruiting | |
St. Louis, Missouri, United States | |
United States, New Hampshire | |
Not yet recruiting | |
Lebanon, New Hampshire, United States | |
United States, New York | |
Not yet recruiting | |
New York City, New York, United States | |
Not yet recruiting | |
Rochester, New York, United States | |
United States, North Carolina | |
Not yet recruiting | |
Charlotte, North Carolina, United States | |
United States, Ohio | |
Not yet recruiting | |
Cincinnati, Ohio, United States | |
Not yet recruiting | |
Columbus, Ohio, United States | |
United States, Oregon | |
Not yet recruiting | |
Portland, Oregon, United States | |
United States, Pennsylvania | |
Not yet recruiting | |
Hershey, Pennsylvania, United States | |
Not yet recruiting | |
Philadelphia, Pennsylvania, United States | |
Not yet recruiting | |
Pittsburgh, Pennsylvania, United States | |
United States, Tennessee | |
Not yet recruiting | |
Memphis, Tennessee, United States | |
Not yet recruiting | |
Nashville, Tennessee, United States | |
United States, Texas | |
Not yet recruiting | |
Dallas, Texas, United States | |
Not yet recruiting | |
Houston, Texas, United States | |
United States, Utah | |
Not yet recruiting | |
Salt Lake City, Utah, United States | |
United States, Vermont | |
Not yet recruiting | |
Burlington, Vermont, United States | |
United States, Washington | |
Seattle Children's Hospital | Recruiting |
Seattle, Washington, United States, 98105 | |
Contact: Ana Christensen 206-884-2756 ana.christensen@seattlechildrens.org | |
Principal Investigator: Susan Apkon, MD |
임상정보는 아래와같습니다.
http://clinicaltrials.gov/ct2/show/study/NCT02255552?term=NCT02255552&rank=1&show_locs=Y#locn
'근육병에 희망을! > Exon Skipping' 카테고리의 다른 글
[DMD, 임상, 임상약품정리]현재 임상중인 약품정리 뉴스 2015 여름 (0) | 2015.07.16 |
---|---|
[DMD,엑손스키핑]약품SRP-4045, SRP-4053 (0) | 2014.10.13 |
[DMD,엑손스키핑]144 주에서 Eteplirsen 데이터 (4) | 2014.07.11 |
[DMD,엑손스키핑.Exon Skipping]Sarepta는 Eteplirsen에 대한 가속 승인을 추구 및 추가 시험을 실시한다 (0) | 2014.05.27 |
[DMD 듀센형]Eteplirsen 아직도 강력한 데이터 : 120 주에서도 안정적 (1) | 2014.02.26 |