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근육병에 희망을!/Exon Skipping

[DMD,엑손스키핑]eteplirsen 3상 임상 참여등록중

Eteplirsen근육 단백질 디스트로핀 유전자의 특정 돌연변이 (결함)가 사람을 치료하는 개발 실험 약물이다.
Sarepta 현재 등록 오픈 여러 사이트를 가지고 있으며, 38 사이트 (PROMOVI 연구라고도 함) 재판에 참여하도록 노력하고 있습니다.


eteplirsen 임상 3차에 참여독려 기사가 올라왔습니다. 엑손스킵 51번입니다.

임상 사이트는 아래와같습니다. 전부 미국지역입니다.


United States, Arizona
Neuromuscular Research CenterRecruiting
Phoenix, Arizona, United States, 85028
Contact: Beth Lasala    480-314-1007    Beth@nrcaz.com   
Principal Investigator: Kumaraswamy Sivakumar, MD         
United States, California
Not yet recruiting
Los Angeles, California, United States
Not yet recruiting
Sacremento, California, United States
Not yet recruiting
San Diego, California, United States
Not yet recruiting
Stanford, California, United States
United States, Colorado
Not yet recruiting
Aurora, Colorado, United States
United States, Connecticut
Not yet recruiting
Hartford, Connecticut, United States
United States, District of Columbia
Not yet recruiting
Washington, District of Columbia, United States
United States, Florida
Not yet recruiting
Gainesville, Florida, United States
Not yet recruiting
Gulf Breeze, Florida, United States
Not yet recruiting
Miami, Florida, United States
Not yet recruiting
Orlando, Florida, United States
United States, Georgia
Not yet recruiting
Atlanta, Georgia, United States
United States, Illinois
Not yet recruiting
Chicago, Illinois, United States
United States, Iowa
University of Iowa Children's HospitalRecruiting
Iowa City, Iowa, United States, 52242
Contact: Carrie Stephan    319-356-2673    carrie-stephan@uiowa.edu   
Principal Investigator: Katherine Mathews, MD         
United States, Kansas
Not yet recruiting
Kansas City, Kansas, United States
United States, Maryland
Not yet recruiting
Baltimore, Maryland, United States
United States, Massachusetts
Not yet recruiting
Boston, Massachusetts, United States
United States, Michigan
Not yet recruiting
Detroit, Michigan, United States
United States, Minnesota
Not yet recruiting
Minneapolis, Minnesota, United States
United States, Missouri
Not yet recruiting
St. Louis, Missouri, United States
United States, New Hampshire
Not yet recruiting
Lebanon, New Hampshire, United States
United States, New York
Not yet recruiting
New York City, New York, United States
Not yet recruiting
Rochester, New York, United States
United States, North Carolina
Not yet recruiting
Charlotte, North Carolina, United States
United States, Ohio
Not yet recruiting
Cincinnati, Ohio, United States
Not yet recruiting
Columbus, Ohio, United States
United States, Oregon
Not yet recruiting
Portland, Oregon, United States
United States, Pennsylvania
Not yet recruiting
Hershey, Pennsylvania, United States
Not yet recruiting
Philadelphia, Pennsylvania, United States
Not yet recruiting
Pittsburgh, Pennsylvania, United States
United States, Tennessee
Not yet recruiting
Memphis, Tennessee, United States
Not yet recruiting
Nashville, Tennessee, United States
United States, Texas
Not yet recruiting
Dallas, Texas, United States
Not yet recruiting
Houston, Texas, United States
United States, Utah
Not yet recruiting
Salt Lake City, Utah, United States
United States, Vermont
Not yet recruiting
Burlington, Vermont, United States
United States, Washington
Seattle Children's HospitalRecruiting
Seattle, Washington, United States, 98105
Contact: Ana Christensen    206-884-2756    ana.christensen@seattlechildrens.org   

Principal Investigator: Susan Apkon, MD            


임상정보는 아래와같습니다.

http://clinicaltrials.gov/ct2/show/study/NCT02255552?term=NCT02255552&rank=1&show_locs=Y#locn